Toggle navigation
Hassan Saei
Home
Projects
Publications
Presentations
Contact
Systematic screening of deep intronic mutational hotspots enables RNA-based personalized therapy in Alport syndrome
Date
Sep 5, 2026
Event
International Workshop on Alport Syndrome
Location
Budapest, Hungary
←
Modeling X-linked Alport syndrome with deep-intronic variations in kidney organoids for antisense oligonucleotide-based therapy development